{"id":588,"date":"2026-03-12T17:26:17","date_gmt":"2026-03-12T16:26:17","guid":{"rendered":"https:\/\/biotechlerncenter.iph-multisite.berta-bewegt.ch\/?page_id=588"},"modified":"2026-03-12T17:26:17","modified_gmt":"2026-03-12T16:26:17","slug":"2-therapie-genique-reparation-dans-le-genome","status":"publish","type":"page","link":"https:\/\/biotechlerncenter.interpharma.ch\/fr\/sujets\/therapie-genique-soigner-les-maladies-a-laide-de-genes\/2-therapie-genique-reparation-dans-le-genome\/","title":{"rendered":"2. Th\u00e9rapie g\u00e9nique: r\u00e9paration dans le g\u00e9nome"},"content":{"rendered":"\n<p>Le terme \u00abth\u00e9rapie g\u00e9nique\u00bb d\u00e9crit bien le principe de base de ce type de traitement: il s\u2019agit de gu\u00e9rir les maladies g\u00e9n\u00e9tiques \u00e0 l\u2019aide de g\u00e8nes r\u00e9parateurs. Les th\u00e9rapies g\u00e9niques qui existent aujourd\u2019hui consistent \u00e0 introduire dans les cellules malades une version saine du g\u00e8ne responsable de la maladie. Celui-ci remplace la fonction du g\u00e8ne d\u00e9fectueux. Une comparaison peut aider \u00e0 comprendre: l\u2019ADN ressemble \u00e0 une route. Si une portion de route est endommag\u00e9e, cela peut causer des maladies. La th\u00e9rapie g\u00e9nique remplace la portion de route ab\u00eem\u00e9e par une portion intacte.<\/p>\n\n\n\n<p>L\u2019id\u00e9e semble simple et en principe, cette approche fonctionne. Mais la mise en \u0153uvre est tout sauf simple. Les effets secondaires \u00e9ventuels du traitement ne sont pas caus\u00e9s par les g\u00e8nes ins\u00e9r\u00e9s dans les cellules mais par la m\u00e9thode employ\u00e9e pour les ins\u00e9rer. Le code g\u00e9n\u00e9tique peut s\u2019en trouver perturb\u00e9, d\u00e9clenchant dans le pire des cas une leuc\u00e9mie.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Le terme \u00abth\u00e9rapie g\u00e9nique\u00bb d\u00e9crit bien le principe de base de ce type de traitement: il s\u2019agit de gu\u00e9rir les maladies g\u00e9n\u00e9tiques \u00e0 l\u2019aide de g\u00e8nes r\u00e9parateurs. Les th\u00e9rapies g\u00e9niques qui existent aujourd\u2019hui consistent \u00e0 introduire dans les cellules malades une version saine du g\u00e8ne responsable de la maladie. Celui-ci remplace la fonction du g\u00e8ne [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":0,"parent":612,"menu_order":1,"comment_status":"closed","ping_status":"closed","template":"page-templates\/unterthema.php","meta":{"_acf_changed":false,"inline_featured_image":false,"footnotes":""},"class_list":["post-588","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO Premium plugin v27.2 (Yoast SEO v27.2) - https:\/\/yoast.com\/product\/yoast-seo-premium-wordpress\/ -->\n<title>2. 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